A 23-year-old man has become the first person in Louisiana to be functionally cured of sickle cell disease through gene therapy, marking a major step forward for treatment in the United States.
Sweden has demonstrated that a single gene therapy injection can restore hearing in people born with a genetic form of deafness, offering a potential long-term treatment.
Landmark gene editing therapy for sickle cell disease patients will soon be available to people with severe forms of the illness across the United Kingdom.
