A 23-year-old man has become the first person in Louisiana to be functionally cured of sickle cell disease through gene therapy, marking a major step forward for treatment in the United States.
Two independent papers praised the new bone marrow transplant method to cure sickle cell disease, a more accessible and less costly procedure than recently approved gene therapies.
Landmark gene editing therapy for sickle cell disease patients will soon be available to people with severe forms of the illness across the United Kingdom.
